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#RareDiseases
BBC 2d

A nine-year-old boy's life has been "fundamentally changed" thanks to approved treatments for spinal muscular atrophy (SMA), allowing him to reach significant milestones like starting mainstream school despite a grim prognosis. #SMA #RareDiseases #HealthcareInnovation #GB

Drug for rare condition 'fundamentally changed' Ramsgate boy's life
BBC 2d

A nine-year-old boy named Ezra, who has spinal muscular atrophy (SMA), has seen his life transformed by treatments recently approved for routine use in the NHS, allowing him to reach milestones that were once thought unattainable after a grim prognosis. #SpinalMuscularAtrophy #RareDiseases #HealthInnovation #GB

Drug for rare condition 'fundamentally changed' Ramsgate boy's life